June 19, 2018

With Tantalizing Early Results, Sarepta’s Gene Therapy for Duchenne Raises Hopes for ‘Real Change’

(STAT News) – An experimental gene therapy for Duchenne muscular dystrophy, licensed to Sarepta Therapeutics, produced jaw-dropping increases in a crucial muscle protein normally missing in patients with the disease, according to preliminary clinical trial data released Tuesday. The data … Read More

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