Gene Therapy Shows Promise for a Growing List of Diseases

November 30, 2017

(NPR) – So far, gene therapy has only been tested on a relatively small number of patients who have been followed for relatively short periods of time. Many more patients will have to be studied for longer periods before anyone really knows how well the therapies work, how long the benefits last, and whether the therapies are safe. But doctors and families of those helped so far are elated at the progress.

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