Gene Therapy for Age-Related Macular Degeneration Safe in Humans
May 18, 2017
(The Scientist) – Wet age-related macular degeneration (AMD) occurs when blood vessels grow and leak fluid into the macula, the central portion of the retina. If left untreated, this condition can lead to vision loss. A new gene therapy that blocks vascular endothelial growth factor (VEGF), a protein that plays a central role in the development of the disease, may be a safe treatment, according to a study published yesterday (May 16) in the Lancet.